A landmark study in China has shown that a base-editing therapy developed by CorrectSequence Therapeutics achieved stellar ...

Now, following up on that success, a large Chinese collaboration has followed up with a description of an improved gene ...

Updated data showed the biotech's approach to the rare lung and liver condition helped restore functional protective proteins in a small study.

University of Virginia School of Medicine scientists have used a next-generation form of gene editing to fix the underlying cause of a severe form of epilepsy in lab mice.

X-linked chronic granulomatous disease (X-CGD) is a rare genetic disorder characterized by high susceptibility to infections that results from genetic mutations in the cytochrome b-245 beta chain ...

In this talk in GEN’s “The State of CRISPR & Genome Editing” virtual summit, originally broadcast on June 11, 2025, Alexis Komor, PhD, Associate Professor at University of California San Diego and ...

Base editors are a type of gene editing tool designed to make precise changes to DNA at the single-nucleotide level. They are used to correct genetic variants that cause disease. 1 This article ...

Durable expression of anti-sickling fetal hemoglobin and reduction in sickle hemoglobin ob ...

Forbes contributors publish independent expert analyses and insights. Juergen Eckhardt leads Bayer’s impact investment unit, Leaps by Bayer. Dr. David Liu, pictured with former lab members Holly Rees ...