The big pharma company will no longer progress emugrobart to late-stage trials in FSHD and SMA due to a lack of efficacy.

Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...

The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...

Tributes flooded the internet for Gilbert Gottfried after his family shared on Tuesday via Twitter that he died following “a long illness.” Since then, there has been more awareness around muscular ...

Genethon, a pioneer and leader in gene therapy for rare diseases, unveiled results at the MDA Conference in Orlando confirming the long-term efficacy of its GNT0004 gene therapy in Duchenne muscular ...

Genentech is halting development of an antibody for two rare genetic diseases after the candidate failed to boost muscle ...

Myotonic muscular dystrophy, which is sometimes called myotonic dystrophy, is a type of muscular dystrophy. There are two types of myotonic muscular dystrophy, described as type 1 (DM 1) and type 2 ...

"While we did see correlations between activity levels and cardiomyopathy progression in patients with Duchenne muscular dystrophy, these correlations were not particularly strong. Our interpretation ...

Mesquite firefighters will be trading their gear for boots — donation boots, that is — as the Mesquite Firefighters ...

Longboat Key firefighters “filled the boot” through a fundraising effort for the Muscular Dystrophy Association.